116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models,...

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Transcript of 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models,...

Page 1: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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Page 2: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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Page 3: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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Page 4: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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Page 5: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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Page 6: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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Page 7: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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Page 8: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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Page 9: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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Page 10: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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Page 11: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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Page 12: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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Page 13: 116Concomitant to these initial safety studies, the efficacy of PTC 124 was tested in mouse models, including a model for cystic fibrosis harboring the CFTR-G542X stop codon mutation

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