Recent Faculty Publications (2012 - 2015) · 2/18/15 Hematology/Oncology Department: Recent Faculty...

2/18/15 Hematology/Oncology Department: Recent Faculty Publications (2012-2015), UCSF Benioff Children's Hospital Oakland

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Hematology/Oncology Department at UCSF Benioff

Children's Hospital Oakland

Recent Faculty Publications (2012 -2015)

Books:

Agrawal AK, Hastings C, Feusner J, eds. Supportive Care in

Pediatric Oncology. Berlin: Springer; 2015.

https://books.google.com/books?id=dSB2oAEACAAJ.

Hastings CA, Torkildson JC, Agrawal AK. Handbook of Pediatric

Hematology and Oncology: Children's Hospital and Research

Center Oakland. Second ed. West Sussex, United Kingdom: John

Wiley & Sons, Ltd.; 2012. http://www.amazon.com/Handbook-

Pediatric-Hematology-Oncology-Childrens/dp/0470670886.

Taher A, Vichinsky E, Musallam K, Cappellini MD, Viprakasit V. Guidelines for the Management

of Non Tranfusion Dependent Thalassemia (NTDT). ed. Cyprus: Thalassemia International

Federation; 2013. http://thalassemia.com/documents/NTDT-TIF-guidelines.pdf.

Vichinsky E, Levine L, Bhatia S, Bojanowski J, Coates T, Foote D, Fung E, Harmatz P, Jeng M,

Knudsen J, Lal A, Pakbaz Z, Schroepfer C, Singer ST, Sweeters N, Walters M, Wood J.

Standards of Care Guidelines for Thalassemia. Oakland, California: Children's Hospital &

Research Center Oakland; 2012.

http://hemonc.cho.org/thalassemia/documents/SOCGuidelines2012.pdf.

Vichinsky E, ed. Emerging Therapies Targeting the Pathophysiology of Sickle Cell Disease.

Hematology/Oncology Cinics of North America 2014/03/05 ed. Philadelphia, PA: Elsevier, Inc.;

2014. http://www.sciencedirect.com/science/journal/08898588/28/2.

Book Chapters:

Agrawal AK. Immunization Practice in Pediatric Oncology. In: Agrawal AK, Hastings CH,

Feusner J, eds. Supportive Care in Pediatric Oncology: A Practical Evidence-Based Approach. Berlin:

Springer; 2015.

Agrawal AK, Feusner J. Supportive Care of Patients with Cancer. In: Lanzkowsky P, Lipton

JM, Fish JD, eds. Manual of Pediatric Hematology and Oncology. 6th ed: Springer; 2015 (in press).

http://www.amazon.com/Handbook-Pediatric-Hematology-Oncology-Childrens/dp/0470670886/

http://www.childrenshospitaloakland.org/main/departments-services/118.aspx

http://facebook.com/CHOHEMONC

https://books.google.com/books?id=dSB2oAEACAAJ

http://www.amazon.com/Handbook-Pediatric-Hematology-Oncology-Childrens/dp/0470670886

http://profiles.ucsf.edu/elliott.vichinsky

http://thalassemia.com/documents/NTDT-TIF-guidelines.pdf


http://hemonc.cho.org/thalassemia/documents/SOCGuidelines2012.pdf


http://www.sciencedirect.com/science/journal/08898588/28/2



Agrawal AK, Hastings C, Feusner J.

Knowledge Gaps and Opportunities for

Research. In: Agrawal AK, Hastings CH,

Feusner J, eds. Supportive Care in Pediatric

Oncology: A Practical Evidence-Based

Approach. Berlin: Springer; 2015.

Agrawal AK, Hord JD. Hematopoietic

Growth Factors. In: Agrawal AK, Hastings

CH, Feusner J, eds. Supportive Care in

Pediatric Oncology: A Practical Evidence-Based Approach. Berlin: Springer; 2015.

Agrawal AK, Shah SS. Pediatrics. In: Gulati A, Puttanniah V, Byas-Smith M, eds. Essentials of

Interventional Cancer Pain Management. New York: Springer; 2015 (in press).

Aguilar A, Agrawal AK, Feusner J. Hyperleukocytosis. In: Agrawal AK, Hastings CH, Feusner J,

eds. Supportive Care in Pediatric Oncology: A Practical Evidence-Based Approach. Berlin: Springer;

2015.

Ataga K, Vichinsky E. Thrombotic complications in sickle cell disease. In: Marder VJ, Aird WC,

Bennett JS, Schulman S, White GC, eds. Hemostasis and Thrombosis: Basic Principles and Clinical

Practice. Chapter 122, Sixth (November 2012) ed. Philadelphia, PA: Lippincott Williams &

Wilkins; 2012:p. 1445. http://books.google.com/books?

id=_SVbYgEACAAJ&dq=9781608319060.

Chung JH, Agrawal AK, Swift PS. Acute Radiation Side Effects. In: Feusner J, Hastings CA,

Agrawal AK, eds. Supportive Care in Pediatric Oncology: A Practical Evidence-Based Approach.

Berlin: Springer; 2015.

DeBaun M, Vichinsky E. Acute pain management in adults with sickle cell disease. In: Basow

DS, ed. UpToDate. Topic 7144 Version 14.0; Oct, 2014. Waltham, MA: UpToDate, Inc.; 2014.

http://www.uptodate.com/contents/acute-pain-management-in-adults-with-sickle-cell-

disease.

DeBaun M, Vichinsky E. Red blood cell transfusion in sickle cell disease. In: Basow DS, ed.

UpToDate. Topic 90145 Version 8.0; Nov 11, 2014. Waltham, MA: UpToDate, Inc.; 2014.

http://www.uptodate.com/contents/red-blood-cell-transfusion-in-sickle-cell-disease.

DeBaun MR, Frei-Jones M, Vichinsky E. Sickle Cell Disease. In: Kliegman R, Stanton BF, St.

Geme J, Schor N, Behrman, eds. Nelson Textbook of Pediatrics, Twentieth Edition. 462.1:

Elsevier, Inc.; 2015 (in press).

Field J, Vichinsky E, DeBaun M. Overview of the management and prognosis of sickle cell

disease. In: Basow DS, ed. UpToDate. Topic 7114 Version 37.0; Dec 01, 2014. Waltham, MD:

UpToDate, Inc.; 2014. http://www.uptodate.com/contents/overview-of-the-management-of-

sickle-cell-disease.

Fung EB, Chung J. Nutrition for Children with Sickle Cell Disease and Thalassemia. In:

Kleinman RE, Greer FR, eds. Pediatric Nutrition Handbook. 7th ed. Elk Grove Village, IL: American

Academy of Pediatrics; 2014:979-92. http://reader.aappublications.org/pediatric-nutrition-7th-

edition-sponsored-member-benefit/2.

Garcia JR, Walters MC. Hematopoietic Cell Transplantation for non-malignant disorders. In:

Greer J, 13th ed., ed. Wintrobe's Clinical Hematology. Philadelphia, PA: Wolwers Kluwer /


http://books.google.com/books?id=_SVbYgEACAAJ&dq=9781608319060


http://www.uptodate.com/contents/acute-pain-management-in-adults-with-sickle-cell-disease


http://www.uptodate.com/contents/red-blood-cell-transfusion-in-sickle-cell-disease



http://www.uptodate.com/contents/overview-of-the-management-of-sickle-cell-disease

http://reader.aappublications.org/pediatric-nutrition-7th-edition-sponsored-member-benefit/2



Lippincott Williams & Wilkins; 2014.

Gomez E, Agrawal AK, Hastings C. Transfusion Support. In: Agrawal AK, Hastings CH, Feusner

J, eds. Supportive Care in Pediatric Oncology: A Practical Evidence-Based Approach. Berlin:

Springer; 2015.

Khurana M, Su W. The Acute Abdomen. In: Feusner J, Hastings CA, Agrawal AK, eds.

Supportive Care in Pediatric Oncology: A Practical Evidence-Based Approach. Berlin: Springer;

2015.

Lalefar NR, Lubin B. Sibling Donor Cord Blood Program: Children�s Hospital Research

Center Oakland and Beyond. In: Dusko I, ed. Stem Cell Banking. New York, NY: Humana

Press/Springer Science; 2014. http://www.amazon.com/Stem-Banking-Biology-Regenerative-

Medicine/dp/1493905848.

Lo CY, Morris CR. Vasculopathy, Chronic Oxidative Stress and Endothelial Dysfunction in

SCD. In: Acu�a-Castroviejo D, Rusanova I, eds. Sickle Cell Disease: A New Vision for an Old

Problem. Recent Advances in Hematology Research. Chapter 5; : Nova Science Publishers;

2013. https://www.novapublishers.co m/catalog/product_info.php?products_id=41344.

Marsh A, Agrawal AK, Feusner J. Tumor Lysis Syndrome. In: Agrawal AK, Hastings CH,

Feusner J, eds. Supportive Care in Pediatric Oncology: A Practical Evidence-Based Approach.

Chapter 3. Berlin: Springer; 2015.

Marsh A, Matsunaga A. Neonatal Alloimmune Thrombocytopenia. In: Cabana MD, ed. The 5-

Minute Pediatric Consult. 7th ed: Lippincott Williams & Wilkins; 2014 (in press).

Marsh A, Vichinsky E. Sickle cell disease. In: Hoffbrand H, Higgs D, Keeling D, Mehta A, eds.

Post Graduate Haematology, 7th edition. Wiley; 2015 (in press).

Morris CR. Arginine and Asthma. In: Makrides M, Ochoa JB, Szajewska H, eds. The Importance

of Immunonutrition. Nestl� Nutrition Institute Workshop Series. Basel, Switzerland: Karger

AG; 2013: pp 1-15 (DOI:0.1159/000351365). http://www.karger.com/Article/Abstract/351365.

Morris CR, Gladwin MT. Pulmonary hypertension in sickle cell disease and thalassemia. In:

Naeije R, Rubin D, eds. Pulmonary Circulation. 4th ed. London, U.K.: Hodder Arnold; 2015 (in

press).

Quirolo K, Vichinsky E. Sickle cell anemia, thalassemia, and other inherited hemolytic

anemia In: Simon TL, McCullough J, Snyder E, Solheim BG, Strauss RG, eds. Rossi's Principles of

Transfusion Medicine, 5th edition. Wiley; 2015 (in process).

Saunthararajah Y, Vichinsky E. Sickle Cell Disease: Clinical Features and Management. In:

Hoffman R, ed. Hematology: Basic Principles and Practice. Chapter 40, 6th ed. Philadelphia, PA:

Saunders/Elsevier; 2013. http://uclibs.org/PID/62059

Vichinsky E. Overview of the clinical manifestations of sickle cell disease. In: Basow DS, ed.

UpToDate. Topic 7119 Version 27.0; Nov. 24, 2014. Waltham, MA: UpToDate, Inc.; 2014.

http://www.uptodate.com/contents/overview-of-the-clinical-manifestations-of-sickle-cell-

disease.

Vichinsky E. Pregnancy in women with sickle cell disease. In: Basow DS, ed. UpToDate. Topic

7139 Version 18.0; Sep 30, 2014. Waltham, MA: UpToDate, Inc.; 2014.

http://www.uptodate.com/contents/pregnancy-in-women-with-sickle-cell-disease.

http://www.amazon.com/Stem-Banking-Biology-Regenerative-Medicine/dp/1493905848

https://www.novapublishers.com/catalog/product_info.php?products_id=41344


http://www.karger.com/Article/Abstract/351365



http://uclibs.org/PID/62059


http://www.uptodate.com/contents/overview-of-the-clinical-manifestations-of-sickle-cell-disease


http://www.uptodate.com/contents/pregnancy-in-women-with-sickle-cell-disease



Vichinsky E. Sickle Cell Syndromes. In: Decision Support in Medicine.

http://decisionsupportinmedicine.com; 2013 (in process).

Vichinsky E. Sickle Cell Trait. In: Basow DS, ed. UpToDate. Topic 7145 Version 24.0; Nov 21

2014. www.UpToDate.com: UpToDate, Inc.; 2014. http://www.uptodate.com/contents/sickle-

cell-trait.

Vichinsky E. Variant Sickle Cell Syndromes. In: Basow DS, ed. UpToDate. Topic 7115 Version

11.0; March 28, 2014. Waltham, MA: UpToDate, Inc.; 2014.

http://www.uptodate.com/contents/variant-sickle-cell-syndromes.

Vichinsky E, Mahoney DH. Diagnosis of sickle cell disorders. In: Basow DS, ed. UpToDate.

Topic 7113 Version 15.0; Aug 28, 2014. Waltham, MA: UpToDate, Inc.; 2014.

http://www.uptodate.com/contents/diagnosis-of-sickle-cell-syndromes.

Walters MC. Hematopoietic cell transplantation for sickle cell disease. In: Forman SJ, Negris

RS, Antin J, Applebaum FR, eds. Hematopoietic Cell Transplantation. Fifth ed. Malden, MA:

Blackwell Science; 2014 (in press).

Journal Articles:

Adam SS, Hoppe C. Potential role for statins in sickle cell disease. Pediatr Blood Cancer

2013;60 4:60;4 p.550-7. http://www.ncbi.nlm.nih.gov/pubmed/23281161.

Afshar M, Birnbaum D, Golden C. Review of dextromethorphan administration in 18 patients

with subacute methotrexate central nervous system toxicity. Pediatr Neurol 2014;50 6:625-

9. http://www.ncbi.nlm.nih.gov/pubmed/24742799.

Afshar M, Golden C. Report of neuroblastoma in a set of monozygotic monochorionic twins.

Pediatr Hematol Oncol 2013;30 4:285-7. http://www.ncbi.nlm.nih.gov/pubmed/23373760.

Afzal SY, Wender AR, Jones MD, Fung EB, Pico EL. The effect of low magnitude mechanical

stimulation (LMMS) on bone density in patients with Rett syndrome: a pilot and feasibility

study. J Pediatr Rehabil Med 2014;7 2:167-78. http://www.ncbi.nlm.nih.gov/pubmed/25096869.

Agrawal AK, Hsu E, Quirolo K, Neumayr LD, Flori HR. Red blood cell transfusion in pediatric

patients with severe chronic anemia: how slow is necessary? Pediatr Blood Cancer 2012;58

3:466-8. http://www.ncbi.nlm.nih.gov/pubmed/21793178.

Agrawal AK, Kammen BF, Guo H, Donthineni R. An unusual presentation of subcutaneous

granuloma annulare in association with juvenile-onset diabetes: case report and literature

review. Pediatr Dermatol 2012;29 2:202-5. http://www.ncbi.nlm.nih.gov/pubmed/22085091.

Aguilar A, Saba JD. Truth and consequences of sphingosine-1-phosphate lyase. Adv Biol

Regul 2012;52 1:17-30. http://www.ncbi.nlm.nih.gov/pubmed/21946005.

Amstrong D, Neumayr L, Gold JI, Weiner MW, Rule RR, LeBeau P, Kesler K, McMahon L, Orringer

EP, Harrington T, DeCastro LM, Kalinyak K, Kutlar A, Rutherford CJ, Johnson C, Bessman JD,

Hussein A, Vichinsky E. Biologic predictors of memory, attention, and executive function in

neurologically asymptomatic adults with sickle cell anemia. 2014 (submitted).

Anglemyer A, Agrawal AK, Rutherford GW. Treatment of Kaposi sarcoma in children with

HIV-1 infection. Cochrane Database Syst Rev 2014;1:CD009826.

http://www.ncbi.nlm.nih.gov/pubmed/24464843.



http://www.uptodate.com/contents/sickle-cell-trait


http://www.uptodate.com/contents/variant-sickle-cell-syndromes


http://www.uptodate.com/contents/diagnosis-of-sickle-cell-syndromes

http://www.ncbi.nlm.nih.gov/pubmed/23281161




http://www.childrenshospitaloakland.org/main/find-a-doctor/468.aspx









Bae HT, Baldwin CT, Sebastiani P, Telen MJ, Ashley-Koch A, Garrett M, Hooper WC, Bean CJ,

Debaun MR, Arking DE, Bhatnagar P, Casella JF, Keefer JR, Barron-Casella E, Gordeuk V, Kato

GJ, Minniti C, Taylor J, Campbell A, Luchtman-Jones L, Hoppe C, Gladwin MT, Zhang Y,

Steinberg MH. Meta-analysis of 2040 sickle cell anemia patients: BCL11A and HBS1L-MYB

are the major modifiers of HbF in African Americans. Blood 2012;120 9:1961-2.


Ballas SK, Kesen MR, Goldberg MF, Lutty GA, Dampier C, Osunkwo I, Wang WC, Hoppe C,

Hagar W, Darbari DS, Malik P. Beyond the definitions of the phenotypic complications of

sickle cell disease: an update on management. ScientificWorldJournal 2012;2012:949535.


Ballas SK, Kesen MR, Goldberg MF, Lutty GA, Dampier C, Osunkwo I, Wang WC, Hoppe C,

Hagar W, Darbari DS, Malik P. Erratum to "Beyond the Definitions of the Phenotypic

Complications of Sickle Cell Disease: An Update on Management". ScientificWorldJournal

2013;2013:861251. http://www.ncbi.nlm.nih.gov/pubmed/23483854.

Ballas SK, Vichinsky E. Is the Medical Home for Adult Patients with Sickle Cell Disease a

Reality or An Illusion? . Hemoglobin 2015 (in press).

Behera RK, Theil EC. Moving Fe2+ from ferritin ion channels to catalytic OH centers

depends on conserved protein cage carboxylates. Proc Natl Acad Sci U S A 2014;111


Bloch EM, Herwaldt BL, Leiby DA, Shaieb A, Herron RM, Chervenak M, Reed W, Hunter R, Ryals

R, Hagar W, Xayavong MV, Slemenda SB, Pieniazek NJ, Wilkins PP, Kjemtrup AM. The third

described case of transfusion-transmitted Babesia duncani. Transfusion 2012;52 7:1517-22.


Chen Q, Fabry ME, Rybicki AC, Suzuka SM, Balazs TC, Etzion Z, de Jong K, Akoto EK, Canterino

JE, Kaul DK, Kuypers FA, Lefer D, Bouhassira EE, Hirsch RE. A transgenic mouse model

expressing exclusively human hemoglobin E: indications of a mild oxidative stress. Blood

Cells Mol Dis 2012;48 2:91-101. http://www.ncbi.nlm.nih.gov/pubmed/22260787.

Chokkalingam AP, Metayer C, Scelo G, Chang JS, Schiffman J, Urayama KY, Ma X, Hansen HM,

Feusner JH, Barcellos LF, Wiencke JK, Wiemels JL, Buffler PA. Fetal growth and body size

genes and risk of childhood acute lymphoblastic leukemia. Cancer Causes Control 2012;23


Cooper TM, Franklin J, Gerbing RB, Alonzo TA, Hurwitz C, Raimondi SC, Hirsch B, Smith FO,

Mathew P, Arceci RJ, Feusner J, Iannone R, Lavey RS, Meshinchi S, Gamis A. AAML03P1, a

pilot study of the safety of gemtuzumab ozogamicin in combination with chemotherapy for

newly diagnosed childhood acute myeloid leukemia: a report from the Children's Oncology

Group. Cancer 2012;118 3:761-9. http://www.ncbi.nlm.nih.gov/pubmed/21766293.

Cui J, Azimi M, Adekile AD, Al Awadhi H, Hoppe CC. Detection of anti-Lepore Hb P-Nilotic by

multiplex ligation-dependent probe amplification. Hemoglobin 2012;36 3:276-82.


Cui J, Azimi M, Baysdorfer C, Vichinsky E, Hoppe CC. Application of multiplex ligation-

dependent probe amplification to screen for beta-globin cluster deletions: detection of two

novel deletions in a multi ethnic population. Hemoglobin 2013;37 3:241-56.
















Cui J, Azimi M, Hoppe CC. Detection of a novel betadelta-globin fusion gene, anti-lepore Hb

CHORI (beta(through IVS-I-57)/delta(from IVS-I-101)), by multiplex ligation-

dependent probe amplification. Hemoglobin 2014;38 1:60-3.


Cui J, Baysdorfer C, Azimi M, Vichinsky E, Hoppe CC. Identification of three novel Hb F

variants: Hb F-Hayward [Ggamma1(NA1)Gly-->Asp, GGT>GAT], Hb F-Chori-I

[AgammaT16(A13)Gly-->Asp, GGC>GAC] and Hb F-Chori-II [AgammaI29(B11)Gly--

>Glu, GGA>GAA]. Hemoglobin 2012;36 3:305-9.


Dagri JN, Evans A, Torkildson JC, Portnow J, Ashby LS, Zakotnik B, Brown RJ, Dhall G, Finlay JL.

Feasibility of an Attenuated Maintenance chemotherapy Regimen Directed at Adolescents

and Young Adults with Newly Diagnosed Localized Medulloblastoma and Other Central

Nervous System Embryonal Tumors. J Adolescent and Young Adult Oncology 2014;3 3:106-11.

Dang DN, Morris HD, Feusner JH, Koduru P, Wilson K, Timmons CF, Cavalier M, Luu HS.

Therapy-induced Secondary Acute Myeloid Leukemia With t(11;19)(q23;p13.1) in a

Pediatric Patient With Relapsed Acute Promyelocytic Leukemia. J Pediatr Hematol Oncol

2014;36 8:e546-8. http://www.ncbi.nlm.nih.gov/pubmed/24942021.

Day LL, Murray E, Treadwell MJ, Lubin BH. Teaching about Genetics and Sickle Cell Disease

in Fifth Grade. Journal of the National Medical Association 2015 (in press).

DeBaun MR, Armstrong FD, McKinstry RC, Ware RE, Vichinsky E, Kirkham FJ. Silent cerebral

infarcts: a review on a prevalent and progressive cause of neurologic injury in sickle cell

anemia. Blood 2012;119 20:4587-96. http://www.ncbi.nlm.nih.gov/pubmed/22354000.

Delgado EM, Cho CS, Gildengorin G, Leibovich SA, Morris CR. Parental Asthma Education and

Risks for Nonadherence to Pediatric Asthma Treatments. Pediatr Emerg Care 2014;30

11:782-7 10.1097/PEC.0000000000000259. http://journals.lww.com/pec-

online/Fulltext/2014/11000/Parental_Asthma_Education_and_Risks_for.3.aspx

Derderian SC, Jeanty C, Walters MC, Vichinsky E, MacKenzie TC. In utero hematopoietic cell

transplantation for hemoglobinopathies. Front Pharmacol 2014;5:278.


Doh I, Lee WC, Cho YH, Pisano AP, Kuypers FA. Deformation measurement of individual cells

in large populations using a single-cell microchamber array chip. Appl Phys Lett 2012;100


Douer D, Zickl LN, Schiffer CA, Appelbaum FR, Feusner JH, Shepherd L, Willman CL, Bloomfield

CD, Paietta E, Gallagher RE, Park JH, Rowe JM, Wiernik PH, Tallman MS. All-trans retinoic acid

and late relapses in acute promyelocytic leukemia: Very long-term follow-up of the North

American Intergroup Study I0129. Leuk Res 2013.


Dror DK, King JC, Durand DJ, Fung EB, Allen LH. Feto-maternal vitamin D status and infant

whole-body bone mineral content in the first weeks of life. Eur J Clin Nutr 2012;66 9:1016-


Dror DK, King JC, Fung EB, Van Loan MD, Gertz ER, Allen LH. Evidence of associations

between feto-maternal vitamin D status, cord parathyroid hormone and bone-specific

alkaline phosphatase, and newborn whole body bone mineral content. Nutrients 2012;4







http://journals.lww.com/pec-online/Fulltext/2014/11000/Parental_Asthma_Education_and_Risks_for.3.aspx








Fens MH, Larkin SK, Oronsky B, Scicinski J, Morris CR, Kuypers FA. The capacity of red blood

cells to reduce nitrite determines nitric oxide generation under hypoxic conditions. PLoS

One 2014;9 7:e101626. http://www.ncbi.nlm.nih.gov/pubmed/25007272.

Flanagan JM, Sheehan V, Linder H, Howard TA, Wang YD, Hoppe CC, Aygun B, Adams RJ, Neale

GA, Ware RE. Genetic mapping and exome sequencing identify two mutations associated

with stroke protection in pediatric patients with sickle cell anemia. Blood 2013.


Fung EB, Gariepy CA, Sawyer AJ, Higa A, Vichinsky E. The effect of whole body vibration

therapy on bone density in patients with thalassemia: a pilot study. Am J Hematol 2012;87

10:E76-9. http://www.ncbi.nlm.nih.gov/pubmed/22886910.

Fung EB, Kwiatkowski JL, Huang JN, Gildengorin G, King JC, Vichinsky E. Zinc supplementation

improves bone density in patients with thalassemia: a double-blind, randomized, placebo-

controlled trial. Am J Clin Nutr 2013;98 4:960-71.


Fung EB, Xu Y, Trachtenberg F, Odame I, Kwiatkowski JL, Neufeld EJ, Thompson AA, Boudreaux

J, Quinn CT, Vichinsky E, Thalassemia Clinical Research N. Inadequate dietary intake in

patients with thalassemia. J Acad Nutr Diet 2012;112 7:980-90.


Gallagher RE, Moser BK, Racevskis J, Poire X, Bloomfield CD, Carroll AJ, Ketterling RP, Roulston

D, Schachter-Tokarz E, Zhou DC, Chen IM, Harvey R, Koval G, Sher DA, Feusner JH, Tallman MS,

Larson RA, Powell BL, Appelbaum FR, Paietta E, Willman CL, Stock W. Treatment-influenced

associations of PML-RARalpha mutations, FLT3 mutations, and additional chromosome

abnormalities in relapsed acute promyelocytic leukemia. Blood 2012;120 10:2098-108.


Garcia JR, Pollard J, Thomson B. Minimal Residual Disease in Acute Leukemias: review of

literature and introduction of �bridging therapy� prior to hematopoietic cell

transplantation. 2014 (submitted).

Gardner K, Hoppe C, Mijovic A, Vichinsky E, Thein SL. How we treat delayed hemolytic

transfusion reactions in patients with sickle cell disease. 2015 (in process).

Gladwin MT, Barst RJ, Gibbs JS, Hildesheim M, Sachdev V, Nouraie M, Hassell KL, Little JA,

Schraufnagel DE, Krishnamurti L, Novelli E, Girgis RE, Morris CR, Berman Rosenzweig E,

Badesch DB, Lanzkron S, Castro OL, Taylor JGt, Goldsmith JC, Kato GJ, Gordeuk VR, Machado

RF, Walk Phaast investigators. Risk factors for death in 632 patients with sickle cell

disease in the United States and United Kingdom. PloS one. 2014;9(7):e99489. Epub

2014/07/06. doi: 10.1371/journal.pone.0099489. PubMed PMID: 24988120; PubMed Central

PMCID: PMC4079316. http://journals.plos.org/plosone/article?

id=10.1371/journal.pone.0099489.

Goldberg SL, Giardina PJ, Chirnomas D, Esposito J, Paley C, Vichinsky E. The palatability and

tolerability of deferasirox taken with different beverages or foods. Pediatr Blood Cancer

2013;60 9:1507-12. http://www.ncbi.nlm.nih.gov/pubmed/23637051.

Gomez E, Morris CR. Asthma Management in Sickle Cell Disease. Biomed Res Int













http://journals.plos.org/plosone/article?id=10.1371/journal.pone.0099489






Green NS, Ender KL, Pashankar F, Driscoll C, Giardina PJ, Mullen CA, Clark LN, Manwani D,

Crotty J, Kisselev S, Neville KA, Hoppe C, Barral S. Candidate sequence variants and fetal

hemoglobin in children with sickle cell disease treated with hydroxyurea. PLoS One 2013;8

2:e55709. http://www.ncbi.nlm.nih.gov/pubmed/23409025.

Green ST, Martin MB, Haines D, Carson S, Coates T, Oliveros O, Gerstenberger E, Trachtenberg

F, Kwiatkowski JL, Thalassaemia Clinical Research N. Variance of pain prevalence and

associated severity during the transfusion cycle of adult thalassaemia patients. Br J

Haematol 2014;166 5:797-800. http://www.ncbi.nlm.nih.gov/pubmed/24805301.

Grigoriev Y, Lange J, Peterson SM, Takashima JR, Ritchey ML, Ko D, Feusner JH, Shamberger

RC, Green DM, Breslow NE. Treatments and outcomes for end-stage renal disease following

Wilms tumor. Pediatr Nephrol 2012;27 8:1325-33.


Haines D, Martin M, Carson S, Oliveros O, Green S, Coates T, Eile J, Schilling L, Dinu B,

Mendoza T, Gerstenberger E, Trachtenberg F, Vichinsky E, Thalassemia Clinical Research N.

Pain in thalassaemia: the effects of age on pain frequency and severity. Br J Haematol


Hastings C, Gaynon PS, Nachman JB, Sather HN, Lu X, Devidas M, Seibel NL. Increased post-

induction intensification improves outcome in children and adolescents with a markedly

elevated white blood cell count (>/=200 x 10 /l) with T cell acute lymphoblastic

leukaemia but not B cell disease: a report from the Children's Oncology Group. Br J

Haematol 2014. http://www.ncbi.nlm.nih.gov/pubmed/25308804.

Hoppe CC. Prenatal and newborn screening for hemoglobinopathies. Int J Lab Hematol


Hoppe CC. Inflammatory mediators of endothelial injury in sickle cell disease. Hematol

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Vichinsky E, Neumayr L, Neuropsych_Study. The Safety and Efficacy of Transfusion

Compared with Standard Care for the Treatment of Neurologic Dysfunction in Adults with

Sickle Cell Disease. 2014 (in process).

Vichinsky E, Neumayr L, Trimble S, Giardina PJ, Cohen AR, Coates T, Boudreaux J, Neufeld EJ,

Kenney K, Grant A, Thompson AA, Investigators CDCT. Transfusion complications in

thalassemia patients: a report from the Centers for Disease Control and Prevention

(CME). Transfusion 2014;54 4:972-81; quiz 1.


Vichinsky E, Torres M, Minniti CP, Barrette S, Habr D, Zhang Y, Files B, study CAi. Efficacy and

safety of deferasirox compared with deferoxamine in sickle cell disease: Two-year results

including pharmacokinetics and concomitant hydroxyurea. Am J Hematol 2013;88 12:1068-


Vichinsky E. The prevention and management of alloimmunization in sickle cell disease: the

benefit of extended phenotypic matching of red blood cells. Immunohematology 2012;28


Vichinsky E. Clinical Manifestations of a-Thalassemia. Cold Spring Harb Perspect Med 2013;(3)

3; 10.1101/cshperspect.a011742.

http://perspectivesmedicine.net/content/early/2013/03/28/cshperspect.a011742.full.pdf+html.

Wagner JE, Jr., Eapen M, Carter S, Wang Y, Schultz KR, Wall DA, Bunin N, Delaney C, Haut P,

Margolis D, Peres E, Verneris MR, Walters M, Horowitz MM, Kurtzberg J, Blood, Marrow

Transplant Clinical Trials N. One-unit versus two-unit cord-blood transplantation for

hematologic cancers. N Engl J Med 2014;371 18:1685-94.


Wahl SK, Garcia A, Hagar W, Gildengorin G, Quirolo K, Vichinsky E. Lower alloimmunization

rates in pediatric sickle cell patients on chronic erythrocytapheresis compared to chronic

simple transfusions. Transfusion 2012;52 12:2671-6.


Wahl SK, Gildengorin G, Feusner J. Weekend delay in initiation of chemotherapy for acute

lymphoblastic leukemia: does it matter? J Pediatr Hematol Oncol 2012;34 1:e8-e11.


Walter PB, Porter J, Evans P, Kwiatkowski JL, Neufeld EJ, Coates T, Giardina PJ, Grady RW,

Vichinsky E, Olivieri N, Trachtenberg F, Alberti D, Fung E, Ames B, Higa A, Harmatz P, Network

TCR. Increased leucocyte apoptosis in transfused beta-thalassaemia patients. Br J Haematol


Wun T, Styles L, DeCastro L, Telen MJ, Kuypers F, Cheung A, Kramer W, Flanner H, Rhee S,

Magnani JL, Thackray H. Phase 1 study of the E-selectin inhibitor GMI 1070 in patients with

sickle cell anemia. PLoS One 2014;9 7:e101301.













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Yamashita R, Sobota A, Trachtenberg F, Xu Y, Pakbaz Z, Odame I, Thompson A, Haines D,

Kleinert D, Giardina P, Quinn C, Kwiatkowski J, Schilling L, Boudreaux J, Neufeld E. The impact

of the child with thalassemia on the family: parental assessments 2014 (in process).

Zaky W, Dhall G, Ji L, Haley K, Allen J, Atlas M, Bertolone S, Cornelius A, Gardner S, Patel R,

Pradhan K, Shen V, Thompson S, Torkildson J, Sposto R, Finlay JL. Intensive induction

chemotherapy followed by myeloablative chemotherapy with autologous hematopoietic

progenitor cell rescue for young children newly-diagnosed with central nervous system

atypical teratoid/rhabdoid tumors: the Head Start III experience. Pediatr Blood Cancer


Zhang L, Samad A, Pombo-de-Oliveria MS, Seelo G, Smith MT, Feusner J, Wiemels JL, Buffler

PA, Metayer C. Global characteristics of childhood acute promyelocytic leukemia. Blood

Reviews 2014;Sep 30 2014.

http://www.sciencedirect.com/science/article/pii/S0268960X14000824 .

Editorials:

Fung EB. Bone health in children with special health care needs. J Pediatr Rehabil Med 2014;7

2:107-9. http://iospress.metapress.com/content/c3231685t0223r84/.

Klings ES, Morris CR. Making it personal: using genomics to predict pulmonary hypertension

in sickle cell disease. Am J Respir Crit Care Med 2012;186 4:304-5.


Vichinsky E. Interventions needed to reduce global burden of sickle cell anemia. HemOnc

Today 2013;14 18:7. http://www.healio.com/hematology-

oncology/hematology/news/online/%7B2e438ef2-647e-4aaa-9c7c-d92b3138b88a

%7D/interventions-needed-to-reduce-global-burden-of-sickle-cell-anemia.

Vichinsky E. Emerging therapy in hemoglobinopathies: lessons from the past and optimism

for the future. Hematol Oncol Clin North Am 2014;28 2:xiii-xviii.


Letters:

Klings ES, Machado RF, Morris CR, Gordeuk VR, Kato GJ, Ataga KI, Castro O, Hsu L, Telen MJ,

Krishnamurti L, Steinberg MH, Gladwin MT, Diagnosis ATSCGft, Treatment of Pulmonary

Hypertension in Sickle Cell Disease C. Reply: Practice guideline for pulmonary hypertension

in sickle cell: direct evidence needed before universal adoption. Am J Respir Crit Care Med.

2014;190(2):238-40. Epub 2014/07/16. doi: 10.1164/rccm.201404-0733LE. PubMed PMID:

25025360; PubMed Central PMCID: PMC4226058. a

href="http://www.atsjournals.org/doi/abs/10.1164/rccm.201404-0733LE#.VLXc-yvF_Tc.

Klings ES, Vichinsky E, Morris CR. Response to "Efficacy and safety of sildenafil for the

treatment of severe pulmonary hypertension in patients with hemoglobinopathies: results

from a long-term follow up " Haematologica 2014;99(2):e17-18. Haematologica 2014;99


Klings ES, Morris CR, Hsu LL, Castro O, Gladwin MT, Mubarak KK. Pulmonary hypertension of

sickle cell disease beyond classification constraints. J Am Coll Cardiol 2014;63 25 Pt A:2881-


http://www.sciencedirect.com/science/article/pii/S0268960X14000824

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http://www.healio.com/hematology-oncology/hematology/news/online/%7B2e438ef2-647e-4aaa-9c7c-d92b3138b88a%7D/interventions-needed-to-reduc%20e-global-burden-of-sickle-cell-anemia



http://www.atsjournals.org/doi/abs/10.1164/rccm.201404-0733LE#.VLXc-yvF_Tc






Reddy-Holdcraft S, Mehta PS, Agrawal AK. Paclitaxel for relapsed or recurrent HIV-

associated pediatric Kaposi's sarcoma. AIDS 2014;28 5:800-2.


Slone JS, Agrawal AK, Mehta PS, Mazhani L, Motumise K, Anabwani G, Poplack DG. Reply to

"Childhood Cancer in Africa". Pediatr Blood Cancer 2014;61 8:1524.


Vichinsky E. Safety of deferasirox in sickle cell disease patients with co-existing liver

impairment -- response to Sinakos et.�al. British Journal of Haematology 2012;157 4:506-7.

http://onlinelibrary.wiley.com/doi/10.1111/j.1365-2141.2012.090 38.x/full.

Abstracts:

Abikoff CM, Talano J-A, Keever-Taylor CA, Walters MC, Shenoy S, Moore T, Parsons SK, Dozor

AJ, Friedman D, Chitti R, Shi Q, Grossman BJ, Weinberg RS, Morris E, Brand P, Foley S, Militano

O, Ayello J, Semidei-Pomales M, Baxter-Lowe LA, Cairo MS. Familial Haploidentical (FHI) T-

Cell Depleted (TCD) with T-Cell Addback Stem Cell Transplantation for Patients with

High-Risk Sickle Cell Disease (SCD) (IND 14359). 56th ASH Annual Meeting and

Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2582.

http://www.bloodjournal.org/content/124/21/2582.

Adams-Graves P, Heeney M, Mueller B, Baltz B, Yang E, Paley C, Esposito J, McNamara K,

Vichinsky E. Treatment patterns and clinical outcomes among patients with sickle cell

disease: 24-month follow-up on a 3-year, prospective, non-interventional registry. ASPHO

27th Annual Meeting. Chicago, IL; May 14-17, 2014. Pediatric Blood & Cancer.

http://aspho.org/uploads/meetings/2014_Abstracts.pdf.

Adisa F, Buchanan I, Morris CR. BiPap use in children with sickle cell disease (SCD) and

acute chest syndrome (ACS). 8th Annual Sickle Cell Disease Research and Education

Symposium. Miami, FL; April 2014.

Aguilar A, Kumar A, Saba J. The effect of sphingadiene treatment on neuroblastoma cells.

Sixth CHORI Research Symposium. Oakland, CA: Mar 30, 2012. Children's Hospital & Research

Center Oakland.

Akinsola B, Hagbom R, Zmitrovich A, Kavanagh P, Ashkouti A, Fletcher A, Vinson N, Simon HK,

Fleming A, Jain S, Adisa O, Dampier C, Morris CR. Adding intranasal fentanyl (INF) to the

management of sickle cell disease (SCD) vaso-occlusive pain episodes (VOE) at a

pediatric emergency department (ED): a quality improvement study. 8th Annual Sickle Cell

Disease Research and Education Symposium. Miami, FL; April 2014.

Akinsola B, Hagbom R, Zmitrovich A, Kavanagh P, Ashkouti A, Fletcher A, Vinson N, Simon HK,

Fleming A, Jain S, Adisa O, Dampier C, Morris CR. More rapid delivery of parenteral analgesia

by adding intranasal fentanyl to the management of sickle cell disease vaso-occlusive

pain episodes at a pediatric emergency department. 56th ASH Annual Meeting and

Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21).

Allard H, Weyhmiller MG, Lal A, Fung EB. In-Accuracy Of Bone Density Measurements By

DXA In Patients With Hemoglobinopathies and Iron Overload. 54th Annual Meeting of the

American Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 966.





http://onlinelibrary.wiley.com/doi/10.1111/j.1365-2141.2012.09038.x/full

http://www.bloodjournal.org/content/124/21/2582


http://aspho.org/uploads/meetings/2014_Abstracts.pdf



http://bloodjournal.hematologylibrary.org/content/12 2/21/966.abstract.

Alter BP, Giri N, Calvo KR, Maric I, Arthur DC, Hickstein DD, Hastings CA, Lee MA, Hsu A, Holland

SM. Clinically Silent Carriers in Families with Myelodysplastic Syndrome Due to GATA2

Mutations. 54th Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11,

2012. Blood 120(21); p.1264. http://abstracts.hematologylibrary.org/cgi/

content/abstract/ashmtg;120/21/1264.

Aydinok Y, Galanello R, Viprakasit V, Piga A, Harmatz P, Forni GL, Shah FT, Grace RF, Porter J,

Vichinsky E, Wood J, Krishnan S, Zhang P, Abi-Saab W, Rienhoff HY, Neufeld E. The safety,

tolerability and efficacy of FBS0701, an iron chelator in clinical development for

transfusional iron overload: data from 72 weeks of treatment. 18th Congress of the

European Hematology Association. Stockholm, Sweden: June 13-16, 2013. Haematologica.

Badawy SM, Pinckney K, Meier ER, Myers K, Black V, Hastings CA, Hilden J, Zweidler-McKay PA,

Stork L, Vaiselbuh SR, Johnson TS. First interim analysis of the ASPHO mentoring program.

ASPHO 27th Annual Meeting. Chicago, IL; May 14-17, 2014.


Calloway C, Lee SH, Kim J, Dhillon N, Gildengorin G, Lal A. Mitochondrial Genome Changes As

a Measure Of Iron-Induced Mitochondrial Stress In Transfusion-Dependent Thalassemia.

55th Annual Meeting of the American Society of Hematology. New Orleans, LA; Dec 7-10,

2013. Blood 122(21); 2256. http://bloodjournal.hematologylibrary.org/content/1

22/21/2256.abstract.

Chung J, Feusner J. Utility of hematologic testing for cases of suspected non-accidental

trauma. ASPHO 25th Annual Meeting. New Orleans, LA; May 9-12, 2012. Pediatric Blood &

Cancer 58(7). http://www.connect2conferenc es.com/aspho4/ws_search/index.php?

task=detail&abstract_id=806.

Chung J, Fung EB, Feusner JH. A Pilot Study to Assess Alterations in Trace Element Status

in Pediatric Patients with Malignancies. 54th Annual Meeting of the American Society of

Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.3183.

http://abstracts.hematologylibrary.org/cgi/ content/abstract/ashmtg;120/21/3183.

Chung J, Lal A, Vichinsky E. Increasing iron overload following splenectomy in Beta

Thalassemia Major. ASPHO Annual Meeting. New Orleans, LA; May 9-12, 2012. Pediatric Blood

& Cancer 58(7); p.1076. http://www.connect2conferenc es.com/aspho4/ws_search/index.php?


Delgado EM, Cho CS, Gildengorin G, Leibovich SA, Morris CR. SPeAK Asthma: A study of

pediatric adherence and knowledge of asthma. Pediatric Academy Society Annual Meeting.

Boston, MA; May 2012.

Fens MHAM, Larkin SK, Fitch WL, Scicinski J, Oronsky B, Kuypers FA. Treatment with a Novel

Dinitroazetidine, Abdnaz, Improves Nitrite Reductase Activity of Sickle Red Blood Cells.

54th Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11, 2012.

Blood 120(21); p.3246. http://abstracts.hematologylibrary.org/cgi/


Fleming A, Jain S, Adisa O, Dampier C, Morris CR. Intranasal fentanyl use improves time to

first parenteral analgesia in children with sickle cell disease vaso-occlusive pain episodes

at a pediatric emergency department. Pediatric Academy Society Annual Meeting. San Diego,

CA; April 2015.

http://bloodjournal.hematologylibrary.org/content/122/21/966.abstract

http://abstracts.hematologylibrary.org/cgi/content/abstract/ashmtg;120/21/1264




http://www.connect2conferences.com/aspho4/ws_search/index.php?task=detail&abstract_id=806







Fung E. Low Magnitude Mechanical Stimulation Increases Bone Mass in Adult Patients with

Thalassemia: A Pilot Study. Sixth CHORI Research Symposium. Oakland, CA: Mar 30, 2012.

Children's Hospital & Research Center Oakland.

Fung EB, Killilea DW, Shenvi S, Haines D, Lavrisha L, Flores B, Higa A, Ahmad T, Lal A. Marginal

zinc status associated with altered insulin metabolism in patients with thalassemia. 4th

International Society for Zinc Biology Meeting. Asilomar, CA; Sep 14-19, 2014. poster

presentation, abstract #FF10.

Fung EB, Kwiatkowski JL, Huang JN, Gildengorin G, King JC, Queisser AC, Vichinsky E. Zinc

supplementation improves bone density in young adults with thalassemia. 6th

International Conference on Children's Bone Health; June 2013. Rotterdam, Netherlands.

Fung EB, Reget K, Sawyer A, Haines D, Lal A. Exploring vertebral abnormalities in patients

with thalassemia and sickle cell disease. 6th International Conference on Children's Bone

Health. Rotterdam, Netherlands; June 2013.

Fung EB, Sushrita N, Haines D, Schroepfer C, Lal A. Dietary Intake Insufficient to Support

Nutritional Adequacy in Patients with Thalassemia. 56th ASH Annual Meeting and

Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 1361-.


Galanello R, Aydinok Y, Piga A, Forni GL, Viprakasit V, Harmatz P, Shah F, Grace R, Vichinsky E,

Wood J, Peppe J, Jones A, Rienhoff HY, Neufeld E. A 48 week phase 2 study of the safety,

tolerability and efficacy of FBS0701, a novel iron chelator for treatment of transfusional

iron overload. 17th Congress of the European Hematology Association. Amsterdam, The

Netherlands: June 14-17, 2012. Haematologica 97(s1); #0606. http://

www.ehaweb.org/congress-and-events/18th-congress/previous-congresses-2/abstract-

book/eha-17-amsterdam-2012/.

Gladwin MT, Barst RJ, Gibbs JS, Hildesheim M, Sachdev V, Nouraie M, Hassell KL, Little JA,

Schraufnagel DE, Krishnamurti L, Novelli E, Girgis RE, Morris CR, Berman Rosenzweig E,

Badesch DB, Lanzkron S, Castro OL, Taylor JGt, Goldsmith JC, Kato GJ, Gordeuk VR, Machado

RF, Walk Phaast investigators. Risk factors for death in 632 patients with sickle cell

disease in the United States and United Kingdom. 54th Annual Meeting of the American

Society of Hematology. Atlanta, GA; Dec 8-11, 2012.

Gomez E, Calloway C, Hoon Lee S, Kim J, Dhillon N, Gildengoren G, Lal A. Mitochondrial

genome changes as a measure of iron-induced mitochondrial stress in transfusion-

depedent thalassemia. 55th Annual Meeting of the American Society of Hematology. New

Orleans, LA; Dec 7-10, 2013. Blood 122(21); 2256.


Hacker NA, King JC, Van Loan MD, Gertz ER, Adams M, Sawyer A, Fung EB. Calcium

supplementation during pregnancy improves tibial bone density at one year post-partum

in racially diverse women. Experimental Biology, April 2014. San Diego, CA. #14-7168.

Haines D. Pain in Thalassemia: Pervasive and Severe. 2nd Meeting of the Worldwide Initiative

on Social Studies on Hemoglobinopathies. Atlanta, GA: March 16, 2012. poster presentation.

Heeney MM, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, Vichinsky E,

George A. Comparison of Clinical Outcomes Between Adult and Pediatric Patients (pts)

with Sickle Cell Disease (SCD): 3-Year (y) Follow-up in a Prospective, Longitudinal,




http://www.ehaweb.org/congress-and-events/18th-congress/previous-congresses-2/abstract-book/eha-17-amsterdam-2012/





Noninterventional Registry Trial. 56th ASH Annual Meeting and Exposition. San Francisco,

CA; Dec 6-9, 2014. Blood 124(21); 4890-. http://www.bloodjournal.org/content/124/21/4890.

Heeney MM, Mueller BU, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, Vichinsky E. 12-

Month Follow-up for Patients with Sickle Cell Disease in an Ongoing 3-Year, Prospective,

Non-Interventional Registry Trial. 54th Annual Meeting of the American Society of



Hoehner C, Hagar RW. A Dedicated Over 50 Sickle Cell Clinic. 6th Annual Sickle Cell Disease

Research and Educational Symposium and Annual National Sickle Cell Scientific Meeting.

Hollywood, Florida; Feb 29-Mar 2, 2012. Am J Hematol 87(7).

http://onlinelibrary.wiley.com/doi/10.1002/ajh.23331/abstrac t.

Jacobs J. Invasive Pulmonary Aspergillosis in Pediatric Oncology Patients. ASPHO 26th

Annual Meeting. Miami, FL; April 24-27, 2013. Pediatric Blood & Cancer 60(S2).

http://www.connect2conferen ces.com/aspho4/ws_search/index.php?


Jubran RF, Leavey PJ, Ritchey AK, Tersak JM, Hastings C, Briones M, Shereck E, Nyquist J,

Fisher D. Career development for pediatric hematology/oncology (PHO) fellows: a pilot

program. ASPHO 26th Annual Meeting. Miami, FL; April 24-27, 2013. Pediatric Blood & Cancer

60(S2). http://www.connect2conferen ces.com/aspho4/ws_search/index.php?


Kamani NR, Walters M, Carter S, Brochstein JA, Eapen M, Levine JE, Logan B, Panepinto J,

Parikh S, Pulsipher M, Schultz KR, Shenoy S. Unrelated Donor Cord Blood Transplantation

For Children With Severe Sickle Cell Disease: Results Of A Phase Ii Study From The Blood

And Marrow Transplant Clinical Trials Network. BMT Tandem Meetings. San Diego, CA: Feb.

1-5, 2012. American Society for Blood and Marrow Transplantation #327.

http://www.abstracts2view.com/bmt/view.php?nu=ASBMT12L_372

Kanathezhath B, Shenvi S, Johl A, Manmohan R, Bhandhal MK, Oh D, Zhou A, Kuypers FA,

Walters MC, Ames BN, Suh J. Systemic And Hepatic Thiol Redox Dysregulation In Graft

Versus Host Disease. BMT Tandem Meetings. San Diego, CA: Feb. 1-5, 2012. American Society

for Blood and Marrow Transplantation #421. http://www.abstracts2view.com/bmt/view.php?

nu=ASBMT12L_259.

Kanathezhath B, Suh J, Shenvi S, Guo H, Walters M, Ames B. Glutathione Redox Metabolomic

Dysregulation Precedes TNF-? Elevation and Predicts Severity of Gvhd in Experimental

Transplantation. BMT Tandem Meetings. Salt Lake City, Utah: Feb. 13-17, 2013. American

Society for Blood and Marrow Transplantation #438.

https://bmt.confex.com/tandem/2013/webprogram/Paper2122.html.

Keller SD, Treadwell MJ, Yang M, Werner EM, Hassell KL. Patient reports of health outcomes

in sickle cell disease: psychometric properties of the Adult Sickle Cell Quality of Life

Measurement System. 2nd Global Congress on Sickle Cell Disease. Rio de Janiero, Brazil:

November 11-14, 2014. http://www.hemorio.rj.gov.br/CongressoGSCDN/programa.pdf.

Khurana M, Feusner JH, Lee B. Fever at diagnosis of pediatric acute lymphoblastic leukemia

(ALL): Are antibiotics really necessary. American Society of Clinical Oncology Annual

Meeting. Chicago, Illinois; June 1-5, 2012. Abstract #9553.

http://meetinglibrary.asco.org/content/101090-114.




http://onlinelibrary.wiley.com/doi/10.1002/ajh.23331/abstract





https://bmt.confex.com/tandem/2013/webprogram/Paper2122.html

http://www.hemorio.rj.gov.br/CongressoGSCDN/programa.pdf

http://meetinglibrary.asco.org/content/101090-114



Khurana M, Kanathezhath B, Feusner J. Recurrent/refractory metastatic osteosarcoma

responds to TRAIL therapy. ASPHO 27th Annual Meeting. Chicago, IL; May 14-17, 2014.


Khurana M, Vichinsky E, Theil EC. Head-to-head comparison of current clinical iron chelators

on cellular ferritin regulation in HEPG2 cell culture model. ASPHO 27th Annual Meeting.

Chicago, IL; May 14-17, 2014. http://aspho.org/uploads/meetings/2014_Abstracts.pdf.

Klein O, Walters M, George D, Chu R, Goodrich JT, Roman E, Schubert R, Del Toro G.

Moyamoya Syndrome Treated With Encephaloduroarteriosynangiosis Followed By

Hematopoietic Cell Transplantation In Patients With Sickle Cell Disease. BMT Tandem

Meetings. San Diego, CA: Feb. 1-5, 2012. American Society for Blood and Marrow Transplantation

#276. http://www.abstracts2view.com/bmt/view.php?nu=ASBMT12L_344

Kutlar A, Reid M, Taher AT, Inati A, Abboud MR, El-Beshlawy A, Buchanan GR, Smith H, Ataga

KI, Koshy N, Neumayr LD, Malik P, Alvarez OA, Ward R, White JM, Johnson E, Ghalie RG. A

Randomized, Open-Label, Multicenter, Dose Escalation Study of HQK-1001 (2,2-

Dimethylbutyrate, Sodium Salt) in Sickle Cell Disease. 54th Annual Meeting of the American

Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.998.

http://abstracts.hematologylibrary.org/cgi/c ontent/abstract/ashmtg;120/21/998.

Kutny MA, Alonzo TA, Gerbing RB, Wang Y-C, Fu C, Meshinchi S, Gamis AS, Feusner JH, Gregory

J. Arsenic Trioxide Is a Well Tolerated Consolidation Regimen in Children with Newly

Diagnosed Acute Promyelocytic Leukemia; Toxicity Results of the Children�s Oncology

Group AAML0631 Trial. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9,

2014. Blood 124(21); 985-. http://www.bloodjournal.org/content/124/21/985.

Kutny MA, Geyer S, Laumann KM, Gregory J, Willman CL, Stock W, Larson RA, Powell BL,

Feusner JH. A Comparison of Outcomes Between Adolescents and Young Adults (AYA) and

Children with Acute Promyelocytic Leukemia (APL): North American Intergroup Study

CALGB 9710 (Alliance). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-

9, 2014. Blood 124(21); 2306-. http://www.bloodjournal.org/content/124/21/2306.

Kutny MA, Geyer S, Laumann KM, Gregory J, Willman CL, Stock W, Larson RA, Powell BL,

Feusner JH. Effect of Young Age on Outcomes in Pediatric Acute Promyelocytic Leukemia

(APL): North American Intergroup Study CALGB 9710 (Alliance). 56th ASH Annual Meeting

and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 2301-.


Kutny MA, Rajpurkar M, Alonzo TA, Gerbing RB, Gamis AS, Feusner JH, Gregory J. Evaluation of

ISTH DIC Score to Predict Significant Bleeding and Thrombosis Events in Pediatric Acute

Promyelocytic Leukemia; A Report from the Children�s Oncology Group AAML0631 Trial.

56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21);

3669-. http://www.bloodjournal.org/content/124/21/3669.

Lal A, Patterson L, Goldrich A, Marsh A, Yen K, Bhatnagar A. Detection of elevated end-tidal

carbon monoxide concentration in children with sickle cell anemia. PAS/ASPR Joint Meeting.

Vancouver, Canada: May 3-6, 2014. Pediatric Academic Societies and Asian Society for Pediatric

Research.

Lal A, Yen K, Patterson L, Goldrich A, Marsh AM, Bhatnagar A. Elevated End-Tidal Carbon

Monoxide Concentration in Children with Sickle Cell Anemia. 56th ASH Annual Meeting and















Lalefar N, Agarwal R, Porteus M, Kharbanda S, Weinberg K. Bortezomib As a Treatment for

Autoimmune Cytopenia After Bone Marrow Transplant. BMT Tandem Meetings. Salt Lake

City, Utah: Feb. 13-17, 2013. American Society for Blood and Marrow Transplantation #125.

Lalefar N, Ozeran J. Iron Overload in Childhood Cancer. ASPHO 25th Annual Meeting. New

Orleans, LA; May 9-12, 2012. Pediatric Blood & Cancer 58(7). http://www.connect2conferenc

es.com/aspho4/ws_search/index.php?task=detail&abstract_id=687.

Lalefar NR, Walters M. Graft failure after hematopoietic cell transplantation for

hemoglobionpathies; successful rescue with alternate donors. Annual Sickle Cell Disease

Research and Educational Symposium and 37th National Sickle Cell Disease Scientific Meeting.

Miami, FL; April 11-14, 2014.

Latronica C, Kuypers FA, Rosenfeld H, Larkin SK, Doniger S, Vichinsky E, Morris CR. Tricuspid

Regurgitant Jet Velocity (TRV), Biomarkers of Hemolysis, and Impact of Oxygen Therapy

in Children with Sickle Cell Disease (SCD) and Vaso-Occlusive Pain Episodes (VOE). 54th

Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood

120(21); p.4752. http://abstracts.hematologylibrary.org/cgi/


Lazarus SG, Adisa O, Zmitrovich A, Hagbom R, Morris CR. Are we missing the mark?

Respiratory signs and symptoms, utilization of chest radiographs (CXRs) and acute chest

syndrome (ACS). Pediatric Academy Society Annual Meeting. San Diego, CA; April 2015.



syndrome (ACS). 8th Annual Sickle Cell Disease Research and Education Symposium. Miami, FL;

April 2014.



syndrome (ACS). 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014.

Blood 124(21).

Lee JH, Rademaker AW, Powell BL, Geyer S, Larson RA, Gregory J, Hijiya N, Feusner JH.

Obesity Does Not Affect the Recurrence Free Survival Rates in Children Less Than 20

Years of Age in Acute Promyelocytic Leukemia (APL). 56th ASH Annual Meeting and



Lew G, Lu X, Yanofsky R, Rheingold SR, Whitlock J, An Q, Devidas M, Hastings CA, Winick NJ,

Carroll WL, Borowitz MJ, Hunger S, Pulsipher MA. Outcomes after Intermediate-Risk Relapse

of Childhood B-Lymphoblastic Leukemia (B-ALL) and the Role of Allogeneic Stem Cell

Transplantation (SCT): A Report from Children's Oncology Group (COG) AALL0433. 56th

ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 684-.


Lew G, Lu X, Yanofsky RA, Rheingold SR, Whitlock JA, Gulig SD, Devidas M, Pulsipher MA,

Hastings CA, Winick NJ, Carroll WL, Borowitz MJ, Hunger SP. The significance of minimal

residual disease (MRD) in relapsed childhood B-lymphoblastic leukemia: Interim analysis

of Children's Oncology Group (COG) protocol AALL0433. ASCO Annual Meeting. Chicago,

IL; May 30-June 3, 2014. J Clin Oncol 32:5s(2014 suppl ); abstr 10014.









Magnani JL, Kuypers FA, Patton JT, Larkin SK, Styles L, DeCastro LM, Telen MJ, Wun T,

Thackray H. Pan-Selectin Antagonist GMI-1070 Affects Biomarkers of Adhesion, Activation

and the Coagulation Cascade in Sickle Cell Adults At Steady State. 54th Annual Meeting of

the American Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.87.

http://abstracts.hematologylibrary.org/cgi/co ntent/abstract/ashmtg;120/21/87.

Majerus EM, Ataga KI, Vichinsky E, Eaton CA, Mazanet R, Nathan DG, Field JJ. NKTT120

Reduces iNKT Cells without Dose Limiting Toxicity in Stable Adult Sickle Cell Patients in a

Phase 1 Trial. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014.

Blood 124(21); 2718-. http://www.bloodjournal.org/content/124/21/2718.

Marsh A, Feusner J, Cham E. Are bone marrow core biopsies necessary for the initial

diagnosis of acute leukemia? ASPHO 25th Annual Meeting. New Orleans, LA; May 9-12, 2012.

Pediatric Blood & Cancer 58(7). http://www.connect2conferenc

es.com/aspho4/ws_search/index.php?task=detail&abstract_id=783.

Marsh AM, Quirolo KC, Golden C, Vichinsky E. Renal Medullary Carcinoma in an Adolescent

with Homozygous Hemoglobin SS. 54th Annual Meeting of the American Society of



Minor M, Harmatz P, Fuentebella J, Haines D, Lal A, Vichinsky E. Practical management of HCV

genotype 1a in B thalassemia major with triple therapy. Viral Hepatitis Congress 2012.

Frankfurt, Germany; Sep 7-9 2012. . Journal of Viral Hepatitis 19(s3); 10. <Go to

ISI>://WOS:000308584500020

Morris CR, Kuypers FA, Lavrisha L, Sweeters N, Stewart M, Ansari M, Neumayr L, Vichinsky EP.

Arginine therapy: a novel treatment for children with sickle cell disease and vaso-

occlusive pain. First Conference of the International Rare Diseases Research Consortium

(IRDiRC). Dublin, Ireland; April 2013.

Morris C, Latronica C, Kuypers FA, Rosenfeld H, Larkin SK, Doniger S, Vichinsky E, Shiva S.

Citrate Synthase Activity Is Increased In Children With Sickle Cell Disease (SCD) On

Hydroxyurea (HU) Therapy. 8th Annual Sickle Cell Disease Research and Education

Symposium. Miami, FL; April 2014.

Morris C, Latronica C, Kuypers FA, Rosenfeld H, Larkin SK, Doniger S, Vichinsky E, Shiva S.

Citrate Synthase Activity Is Increased In Children With Sickle Cell Disease (SCD) On

Hydroxyurea (HU) Therapy. 55th Annual Meeting of the American Society of Hematology.

New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 4690.


Morris CR, Barreda F, Leibovich SA, Rutherford M, Saulys A, Stewart M, Lavrisha L, Vichinsky E,

Bell M, Treadwell MJ. Quality Improvement Goals for Sickle Cell Disease Pain Management

in an Urban Pediatric Emergency Department: We Can Do Better! 54th Annual Meeting of

the American Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.2101.


Morris CR, Barreda F, Leibovich SA, Rutherford M, Saulys A, Stewart M, Lavrisha L, Vichinsky E,

Bell M, Treadwell MJ. Quality improvement initiatives for sickle cell disease pain

management in an urban pediatric emergency department significantly improves

outcomes. Pediatric Academic Societies Annual Meeting; May 4-7, 2013. Washington, DC.

http://www.abstracts2view.com/pas/view.php?nu=PAS13L1_4523. 443.














http://www.abstracts2view.com/pas/view.php?nu=PAS13L1_4523.443



Morris CR, Kim H-Y, Wood JC, Trachtenberg F, Klings ES, Porter JB, Sweeters N, Olivieri NF,

Kwiatkowski JL, Singer ST, Taher AT, Neufeld EJ, Thompson AA, Larkin SK, Suh JH, Vichinsky E,

Kuypers FA. Cardiopulmonary and Laboratory Profiling of Patients with Thalassemia At

Risk for Pulmonary Hypertension: Report From the Thalassemia Clinical Research

Network. 54th Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11,



Morris CR, Kim H-Y, Wood JC, Trachtenberg F, Klings ES, Porter JB, Sweeters N, Olivieri NF,

Kwiatkowski JL, Singer ST, Taher AT, Neufeld EJ, Thompson AA, Sachdev V, Larkin SK, Suh JH,

Kuypers FA, Vichinsky E. Sildenafil Therapy in Patients with Thalassemia and an Elevated

Tricuspid Regurgitant Jet Velocity (TRV) On Doppler Echocardiography At Risk for

Pulmonary Hypertension: Report From the Thalassemia Clinical Research Network. 54th

Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood

120(21); p.1023. http://abstracts.hematologylibrary.org/cgi/


Morris CR, Kuypers FA, Lavrisha L, Sweeters N, Stewart M, Ansari M, Neumayr L, Vichinsky EP.

Randomized, placebo-controlled trial of arginine therapy for the treatment of children with

sickle cell disease and vaso-occlusive pain episodes. NHLBI workshop: Translating new

therapeutics for sickle cell disease to the marketplace; August 21, 2013; National Institutes of

Health, Bethesda MD.

Morris HD, Feusner JH, Wilson KS, Aquino V, Levenson B, Timmons M, Cavalier M, Luu H.

Therapy-induced t(11;19)(q23;q13.1) with relapsed acute promyelocytic leukemia.

ASPHO 26th Annual Meeting. Miami, FL; April 24-27, 2013. Pediatric Blood & Cancer 60(S2); 895.

http://www.connect2conferenc es.com/aspho4/ws_search/index.php?


Morris HD, Feusner JH, Wilson KS, et.al. Therapy-induced t(11;19)(q23;q13.1) with

relapsed acute promyelocytic leukemia. Association of Molecular Pathology Annual Meeting.

May 2012.

Mueller BU, Baltz B, Adams-Graves P, Yang E, Paley C, MSHS JE, MSHS CCRA MK, Vichinsky E.

Clinical Outcomes For Patients With Sickle Cell Disease: 24-Month Follow-Up In An

Ongoing 3-Year, Prospective, Non-Interventional Registry Trial. 55th Annual Meeting of

the American Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 988.


Murray L, Walters MC, Chaudhury S, Soni S, Pulsipher MA, Schultz KR, Chan K, Nieder M,

Loechelt B, Parikh SH, Kasow KA, Haight A, Hale GA, Connelly J, Andreansky M, Trachtenberg F,

Neufeld EJ, Kwiatkowski J, DiFronzo NL, Thompson AA. Multicenter Investigation Of

Unrelated Donor Hematopoietic Cell Transplantation (HCT) For Thalassemia Major After a

Reduced Intensity Conditioning Regimen (URTH Trial). 55th Annual Meeting of the American

Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 543.


Novelli EM, Delaney K, Axelrod K, Morris CR, Minniti C. Arginine therapy in a patient with Hb-

SS disease and refractory leg ulcers. Sickle Cell Disease Association of America Annual

Convention. Baltimore, MD; Sept 2012.

Paulukonis S, Currier R, Coates TD, Vichinsky E, Feuchtbaum L. Impact of Immigration and

Migration on Thalassemia Surveillance in California, 2004-2008. 56th ASH Annual Meeting












and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 4855-.


Paulukonis S, Griffin T, Zhou M, Eckman JR, Hagar R, Bauer Snyder A, Feuchtbaum L, Grant AM,

Hulihan M. Sickle Cell Disease Mortality in California and Georgia 2004-2008. 56th ASH

Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 439-.


Porter J, Walter PB, Neumayr LD, Evans P, Weyhmiller MG, Harmatz P, Wood JC, Miller JL,

Weiss G, Yuan Q, Wang ZJ, Grosse R, Schoennagel BP, Meerpohl J, Fischer R, Nielsen P, Seifert

M, Vichinsky E. Inflammatory and Vitamin Bio-Markers Of Iron Trafficking and Distribution

In Transfusional Overload: Insights From Comparing Diamond Blackfan Anemia With

Sickle Cell Disease and Thalassemia (MCSIO PILOT Study). 55th Annual Meeting of the



Porter JB, Walter PB, Neumayr LD, Evans P, Weyhmiller MG, Harmatz P, Wood JC, Miller JL,

Weiss G, Yuan Q, Wang ZJ, Grosse R, Schoennagel BP, Meerpohl J, Fischer R, Seifert M,

Vichinsky E. Bio-markers of Iron Trafficking and Distribution in Transfusional Overload:

Insights from Comparing Diamond Blackfan Anemia with Sickle Cell Disease and

Thalassemia (MCSIO Pilot Study). International BioIron Society Meeting. University College

London; April 14-18, 2013.

Porter JB, Walter PB, Neumayr LD, Evans P, Weyhmiller MG, Harmatz P, Wood JC, Miller JL,

Weiss G, Yuan Q, Wang ZJ, Grosse R, Schoennagel BP, Meerpohl J, Fischer R, Vichinsky E. Iron

Trafficking and Distribution in Transfusional Overload: Insights From Comparing Diamond

Blackfan Anemia with Sickle Cell Disease and Thalassemia. 54th Annual Meeting of the

American Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.995.

http://abstracts.hematologylibrary.org/cgi/c ontent/abstract/ashmtg;120/21/995.

Radhakrishnan K, Talano J, Keever-Taylor C, Bhatia M, Shenoy S, Walters M, Parsons S, Morris

E, Baxter-Lowe LA, Cairo MS. Familial Haploidentical (FHI) T-Cell Depleted (TCD)

Transplantation In High-Risk Sickle Cell Disease (IND 14359). BMT Tandem Meetings. San

Diego, CA: Feb. 1-5, 2012. American Society for Blood and Marrow Transplantation #265.


Schiffelers R, Gildengorin G, Kuypers FA, Hoppe C. Microparticles As Biomarkers Of

Osteonecrosis Of The Hip In Sickle Cell Disease. 55th Annual Meeting of the American

Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 2226.


Singer ST, Wang J, Suh JH, Killelea D, Ivani K, Oliveros O, Yuan Q, Vichinsky E, Smith J.

Abnormal Reproductive Measures and Seminal Plasma Findings in Men With Thalassemia

Major (TM) and Iron Overload. 55th Annual Meeting of the American Society of Hematology.

New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 4707.


Singer ST, Wang J, Yuan Q, Vichinsky E, Smith J, Paley C, Fischer R. Pituitary Iron and Volume

Are Affecting Hormones and Reproductive Potential. 56th ASH Annual Meeting and

Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 4048.

https://ash.confex.com/ash/2014/webprogram/Paper75574.html.

Suh JH, Kanathezhath B, Swapna S, Guo H, Walters MC, Ames BN. Host Nrf2 -glutathione
















https://ash.confex.com/ash/2014/webprogram/Paper75574.html



Redox Dysregulation Precedes TNF-{alpha} Elevation and Predicts Severity of Graft

Versus Host Disease in Experimental Transplantation. 54th Annual Meeting of the American

Society of Hematology. Atlanta, GA; Dec 8-11, 2012. Blood 120(21); p.4107.


Thompson AA, Rasko JE, Hongeng S, Kwiatkowski JL, Schiller G, von Kalle C, Cavazzana M,

Leboulch P, Petrusich A, Soni S, Walters MC. Initial Results from the Northstar Study (HGB-

204): A Phase 1/2 Study of Gene Therapy for ?-Thalassemia Major Via Transplantation of

Autologous Hematopoietic Stem Cells Transduced Ex Vivo with a Lentiviral ??-T87Q -

Globin Vector (LentiGlobin BB305 Drug Product). 56th ASH Annual Meeting and Exposition.

San Francisco, CA; Dec 6-9, 2014. Blood 124(21); 549. Nominated for Best of ASH abstract.


Treadwell M, Paulukonis S, Currier B, Hutchinson C, Neumayr L, Vichinsky E, Feuchtbaum L.

Population-based study of mental health diagnoses and utilization in sickle cell disease.

Annual Sickle Cell Disease Research and Educational Symposium and 37th National Sickle Cell

Disease Scientific Meeting. Miami, FL; April 11-14, 2014. poster presentation.

Treadwell M, Johnson S, Sisler I, Gildengorin G, Medina R, Barreda F, Bitsko M, Smith WR.

Evaluation of a sickle cell disease specific readiness for transition assessment. 8th Annual

Sickle Cell Disease Research & Educational Symposium and 37th National Sickle Cell Disease

Scientific Meeting. Miami, FL. April 11-14, 2014. Journal of Sickle Cell Disease and

Hemoglobinopathies 2014(1; doi 10.14223/JSCDH-D-14-00081).

Treadwell MJ, Anie K, Asafo M, Creary M, Dennis-Atwi J, grant A, Lamptey M, Ojodu J, Otaigbe

A, Yusuf C, Ohene-Frempong K. Development Workshop for a Sickle Cell Counselor Training

and Certification Program in Ghana. SCDAA 41st Annual Convention; Sept 25-27, 2013.

Baltimore, MD.

Treadwell MJ, Barreda F, Payton W, Sydnor V, Murphy W. Using Multidimensional Strategies

to Improve Adherence with Iron Chelation Therapies. SCDAA 41st Annual Convention; Sept

25-27, 2013. Baltimore, MD.

Treadwell MJ, Bell M, Leibovich SA, Barreda F, Marsh A. Quality improvement initiative

improves emergency department care for pediatric patients with sickle cell disease. UCSF

Seventh Annual Health Disparities Research Symposium. Oct 23, 2013; San Francisco, CA.

Trobaugh-Lotrario AD, Chaiyachati BH, Meyers R, Haberle B, Tomlinson GE, Katzenstein HM,

Malogolowkin MH, von Schweinitz D, Krailo MD, Feusner JH. Outcome in congenital

hepatoblastoma compared with previously reported data. 2013 ASCO Annual Meeting. May

30 - Jun 3, 2014; Chicago, Illinois. American Society of Clinical Oncology.

http://meetinglibrary.asco.org/content/118312-132.

Vichinsky E. Fetal hemoglobin and its relationship to CNS disease in hemoglobinopathies.

18th Annual Hemoglobin Switching Conference. Monterey, California; June 7-11, 2012.

Vichinsky E, Baltz B, Adams-Graves P, Yang E, Paley C, Esposito J, McNamara K, George A,

Heeney MM. Clinical complications in pediatric and adult sickle cell disease. Association of

Pediatric Hematology/Oncology Nurses (APHON) Annual Conference & Exhibit. Portland, OR; Sep

4-6 2014. poster presentation.

Vichinsky E, Beshlawy AE, Alzoebie A, Bernaudin F, Koussa S, Chotsampancharoen T, El-Ali A,

Arrowsmith C, Martin M, El-Alfy M. Long-term safety and effectiveness of deferasirox

(Exjade�) in pediatric patients aged 2�<6 years at enrollment: Interim report from a 5-





http://meetinglibrary.asco.org/content/118312-132






year observational study. 3rd Pan-European Conference on Haemoglobinopathies and Rare

Anaemias. Limassol, Cyprus: Oct 24-26, 2012.

Vichinsky E, El-Beshlawy A, Alzoebie A, Bernaudin F, Koussa S, Chotsampancharoen T, El-Ali A,

Arrowsmith C, Martin N, El-Alfy M. Interim Safety and Effectiveness Results From a 5-Year

Observational Study of Deferasirox in Pediatric Patients Aged 2-<6 Years At Enrollment.

54th Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11, 2012.

Blood 120(21); p.2125. http://abstracts.hematologylibrary.org/cgi/


Vichinsky E. Neuropsychological Dysfunction And Neuroimaging Abnormalities In

Neurologically Intact Adults with SCD. 6th Annual Sickle Cell Disease Research and

Educational Symposium and Annual National Sickle Cell Scientific Meeting. Hollywood, Florida;

Feb 29-Mar 2, 2012. oral presentation.

Vichinsky E. Clinical Aspects of Iron Overload: Causes, Diagnosis, Complications,

Treatment, Outcomes. Society for Pediatric Radiology 55th Annual Meeting & Postgraduate

Course. San Francisco, California; April 19, 2012. Pediatr Radiol 42, Issue 2 Supplement(2);

oral presentation. http://link.springer.com.ucsf.idm.oclc.org/article/10.1007/s00247-012-2356-

8/fulltext.html.

Walter PB, Harmatz P, Higa A, Ng V, Weyhmiller MG, Evans P, Porter JB, Sweeters N, Price J,

Manji A, Killilea D, Lal A, Vichinsky E. Innate Immune Cell Expression of Pattern Recognition

Receptors From {beta}-Thalassemia Patients During Intensive Combination Chelation

Therapy. 54th Annual Meeting of the American Society of Hematology. Atlanta, GA; Dec 8-11,



Walter PB, Harmatz P, Higa A, Ng V, Weyhmiller MG, Evans P, Porter JB, Sweeters N, Price J,

Manji A, Killilea D, Lal A, Vichinsky E. Innate Immune Cell Expression of Pattern Recognition

Receptors from Transfused Thalassemia Major Patients During Intensive Combination

Chelation Therapy. International BioIron Society Meeting. University College London; April 14-

18, 2013.

Walter PB, Higa A, Ng V, Weyhmiller MG, Slater NR, Evans P, Porter JB, Sweeters N, Price J,

Manji A, Killilea D, Lal A, Vichinsky E. Association Of Cardiac Iron By T2* With Innate

Immune Markers In Transfusion-Dependent Thalassemia Patients Undergoing Combined

Chelation Therapy. 55th Annual Meeting of the American Society of Hematology. New



Walter PB, Pakbaz Z, Nemeth E, Ganz T, Porter JB, Evans P, Houston KM, Fischer R, Weyhmiller

MG, Herz M, Miller JL, Hagar R, Neumayr LD, Vichinsky E, Harmatz P. Determinants Of Tissue

Iron Loading In Transfused and Non-Transfused ?-Thalassemia and Sickle Cell Disease

Patients � Biomarkers Of Iron Regulation and Inflammation. 55th Annual Meeting of the



Walter PB, Hohman L, Rokeby A, Manocha A, Lum JJ, Lavrisha L, Stewart M, Hagar R, Vichinsky

E, Morris CR. The effects of glutamine supplementation on markers of autophagy and

apoptosis in peripheral blood mononuclear cells from patients with sickle cell disease. Free

Radical Biology and Medicine. Seattle, WA; Nov 2014.





http://link.springer.com.ucsf.idm.oclc.org/article/10.1007/s00247-012-2356-8/fulltext.html











Walter PB, Hohman L, Rokeby A, Manocha A, Lum JJ, Lavrisha L, Stewart M, Hagar R, Vichinsky

E, Morris CR. The effects of glutamine supplementation on markers of autophagy and

apoptosis in peripheral blood mononuclear cells from patients with sickle cell disease.

56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood 124(21).

Walters MC, Sandmaier BM, Storb R, D. Flowers ME, Deeg HJ, O'Donnell P, Woolfrey AE, Kiem

H-P. Modulated Cyclophosphamide-Based In Vivo T-Cell Depletion Promotes Engraftment

With Minimal Gvhd and Low Toxicity In Fanconi Anemia Patients. 55th Annual Meeting of

the American Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood 122(21); 4561.


Wang J, Suh JH, Killelea D, Ivani K, Oliveros O, Yuan Q, Vichinsky E, Smith J. Abnormal

Reproductive Measures and Seminal Plasma Findings in Men With Thalassemia Major

(TM) and Iron Overload. 55th Annual Meeting of the American Society of Hematology. New



Wang Z, Diaw L, Dizon M, Barr M, Quinn M, Diggs D, Allen D, Seamon C, Oguhebe A, Darbari D,

Zhang Y, Gladwin MT, Hutchinson AA, Burdette L, Hoppe C. Admixture In Sickle Cell Disease

Defined By Genome Wide Ancestry Informative Markers Varies By Geographic Region In

The United States. 55th Annual Meeting of the American Society of Hematology. New Orleans,

LA; Dec 7-10, 2013. Blood 122(21); 995. http://bloodjournal.hematologylibrary.org/content/12

2/21/995.abstract.

Wang ZJ, Wood JC, Walter PB, Schoennagel BP, Evans P, Neumayr LD, Weyhmiller MG,

Harmatz P, Moon JC, Yuan Q, Miller JL, Weiss G, Grosse R, Meerpohl J, Nielsen P, Vichinsky E,

Porter JB, Fischer R. Iron distribution assessed by MRI in sickle cell disease, thalassemia

and Diamond Blackfan Anemia (MCSIO Pilot Study). International BioIron Society Meeting.

University College London; April 14-18, 2013.

Weisdorf DJ, Guethlein LA, Klein JP, Wang T, Marsh SGE, Spellman S, Haagenson MD, Saeturn

K, Ladner M, Trachtenberg E, Parham P, Miller JS. Recipient HLA-C1 Enhances The Clinical

Advantage Of Killer-Cell Immunoglobulin-Like Receptor B haplotype Donors In

Myeloablative Unrelated Transplantation For Acute Myelogenous Leukemia. 54th Annual

Meeting of the American Society of Hematology. New Orleans, LA; Dec 7-10, 2013. Blood

122(21); 549. http://bloodjournal.hematologylibrary.org/content/12 2/21/549.abstract.

Wun T, Telen MJ, Krishnamurti L, McCavit TL, DeCastro LM, Flanner H, Kuypers FA, Larkin SK,

Rhee S, Magnani JL, Thackray HM. Pan-Selectin Antagonist Rivipansel (GMI-1070) Reduces

Soluble E-Selectin Levels While Improving Clinical Outcomes in SCD Vaso-Occlusive

Crisis. 56th ASH Annual Meeting and Exposition. San Francisco, CA; Dec 6-9, 2014. Blood

124(21); 2704. http://www.bloodjournal.org/content/124/21/2704.

Yang E, Baltz B, Adams-Graves P, Paley C, Esposito B, Vichinsky E. 12-month follow-up for

patients with sickle cell disease in an ongoing 3-year prospective, non-interventional

registry trial. SCDAA 41st Annual Convention; Sept 25-27, 2013. Baltimore, MD.

Yesim A, Galanello R, Viprakasit V, Piga A, Harmatz P, Forni GL, Shah F, Grace R, Porter J,

Vichinsky E, Wood J, Krishnan S, Zhang P, Abi-Saab W, Rienhoff HY, Neufeld E. The safety,

tolerability and efficacy of FBS0701, an iron chelator in clinical development for

transfusional iron overload: Data from 72 weeks of treatment. 18th Congress of the

European Hematology Association. Stockholm, Sweden; June 13-16, 2013.













updated 18 Feb 2015

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Recent Faculty Publications (2012 - 2015) · 2/18/15 Hematology/Oncology Department: Recent Faculty...

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